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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of Olezarsen for the Treatment of Familial Chylomicronemia Syndrome (FCS) in Pediatric Participantsfamilial chylomicronemia syndrome, familial lipoprotein lipase deficiencyRecruitingPhase 32026-10-08NCT07727538
CS-121 APOC3 Base Editing in FCSDigestive System Diseases, Dyslipidemias, Lipid Metabolism Disorders, Nutritional and Metabolic Diseases, familial lipoprotein lipase deficiency, hyperlipidemia, hypertriglyceridemia, metabolic disease, pancreas disorder, pancreatitisRecruitingEarly phase 12026-02-11NCT07176923
Postprandial Fatty Acid Metabolism in Subjects With Lipoprotein Lipase DeficiencyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, familial lipoprotein lipase deficiency, hereditary disease, hyperlipidemia, hyperlipoproteinemia, inborn errors of metabolism, metabolic diseaseRecruitingNot applicable2026-02-10NCT04227678
CS-121 APOC3 Base Editing in Children and Adolescents With HyperchylomicronemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Dyslipidemias, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, familial lipoprotein lipase deficiency, hereditary disease, hyperlipidemia, hyperlipoproteinemia, inborn errors of metabolism, metabolic disease, pancreas disorder, pancreatitisRecruitingEarly phase 12026-01-28NCT07371767
Study of RN0361in Adult Healthy Subjects and Adult Hypertriglyceridemic SubjectsDyslipidemias, Lipid Metabolism Disorders, Nutritional and Metabolic Diseases, familial chylomicronemia syndrome, familial lipoprotein lipase deficiency, hyperlipidemia, hypertriglyceridemia, metabolic diseaseActive, not recruitingPhase 1 / Phase 22025-12-30NCT06471543
A Study of Olezarsen (Formerly Known as AKCEA-APOCIII-LRX) Administered to Adults With Familial Chylomicronemia Syndrome (FCS) Previously Treated With Volanesorsenfamilial chylomicronemia syndrome, familial lipoprotein lipase deficiencyActive, not recruitingPhase 32025-12-12NCT05185843
A Study of Olezarsen (Formerly Known as AKCEA-APOCIII-LRx) in Participants With Familial Chylomicronemia Syndrome (FCS)familial chylomicronemia syndrome, familial lipoprotein lipase deficiencyActive, not recruitingPhase 32025-12-12NCT05130450