familial lipoprotein lipase deficiency
familial lipoprotein lipase deficiency
Explore linked clinical trials. Standard reference: MONDO:00093877 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study of Olezarsen for the Treatment of Familial Chylomicronemia Syndrome (FCS) in Pediatric Participants | familial chylomicronemia syndrome, familial lipoprotein lipase deficiency | Recruiting | Phase 3 | 2026-10-08 | NCT07727538 | |
| CS-121 APOC3 Base Editing in FCS | Digestive System Diseases, Dyslipidemias, Lipid Metabolism Disorders, Nutritional and Metabolic Diseases, familial lipoprotein lipase deficiency, hyperlipidemia, hypertriglyceridemia, metabolic disease, pancreas disorder, pancreatitis | Recruiting | Early phase 1 | 2026-02-11 | NCT07176923 | |
| Postprandial Fatty Acid Metabolism in Subjects With Lipoprotein Lipase Deficiency | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, familial lipoprotein lipase deficiency, hereditary disease, hyperlipidemia, hyperlipoproteinemia, inborn errors of metabolism, metabolic disease | Recruiting | Not applicable | 2026-02-10 | NCT04227678 | |
| CS-121 APOC3 Base Editing in Children and Adolescents With Hyperchylomicronemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Dyslipidemias, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, familial lipoprotein lipase deficiency, hereditary disease, hyperlipidemia, hyperlipoproteinemia, inborn errors of metabolism, metabolic disease, pancreas disorder, pancreatitis | Recruiting | Early phase 1 | 2026-01-28 | NCT07371767 | |
| Study of RN0361in Adult Healthy Subjects and Adult Hypertriglyceridemic Subjects | Dyslipidemias, Lipid Metabolism Disorders, Nutritional and Metabolic Diseases, familial chylomicronemia syndrome, familial lipoprotein lipase deficiency, hyperlipidemia, hypertriglyceridemia, metabolic disease | Active, not recruiting | Phase 1 / Phase 2 | 2025-12-30 | NCT06471543 | |
| A Study of Olezarsen (Formerly Known as AKCEA-APOCIII-LRX) Administered to Adults With Familial Chylomicronemia Syndrome (FCS) Previously Treated With Volanesorsen | familial chylomicronemia syndrome, familial lipoprotein lipase deficiency | Active, not recruiting | Phase 3 | 2025-12-12 | NCT05185843 | |
| A Study of Olezarsen (Formerly Known as AKCEA-APOCIII-LRx) in Participants With Familial Chylomicronemia Syndrome (FCS) | familial chylomicronemia syndrome, familial lipoprotein lipase deficiency | Active, not recruiting | Phase 3 | 2025-12-12 | NCT05130450 |