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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
CS-121 APOC3 Base Editing in Children and Adolescents With HyperchylomicronemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Dyslipidemias, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, familial lipoprotein lipase deficiency, hereditary disease, hyperlipidemia, hyperlipoproteinemia, inborn errors of metabolism, metabolic disease, pancreas disorder, pancreatitisRecruitingEarly phase 12026-01-28NCT07371767

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Research sitesCityCountryLinked trials
Shanghai Children's Medical CenterShanghaiChina4