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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Nucleoside Therapy in Patients With Telomere Biology DisordersBone Marrow Failure Disorders, Congenital Abnormalities, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fibrosis, Hemic and Lymphatic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Revesz syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, X-linked disease, bone marrow disorder, dyskeratosis congenita, hematologic disorder, hereditary disease, hereditary skin disorder, interstitial lung disease, lung disorder, pulmonary fibrosis, respiratory system disorder, skin disorderRecruitingPhase 12026-08-04NCT06817590
Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis CongenitaBone Marrow Failure Disorders, Congenital Abnormalities, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Revesz syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, X-linked disease, anemia, aplastic anemia, bone marrow disorder, dyskeratosis congenita, hematologic disorder, hereditary disease, hereditary skin disorder, skin disorderActive, not recruitingPhase 22026-03-27NCT01659606