Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita
Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita
Active, not recruiting · NCT01659606 · Registry updated 2026-03-27Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita | Bone Marrow Failure Disorders, Congenital Abnormalities, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Revesz syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, X-linked disease, anemia, aplastic anemia, bone marrow disorder, dyskeratosis congenita, hematologic disorder, hereditary disease, hereditary skin disorder, skin disorder | Active, not recruiting | Phase 2 | 2026-03-27 | NCT01659606 |
13 results · Page 1 of 1
Organizations
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13 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Baylor College of Medicine | Houston | United States | 306 |
| Boston Children's Hospital (pediatric patients) | Boston | United States | 1 |
| Children's Hospital of Philadelphia | Philadelphia | United States | 434 |
| Children's Mercy Hospital Kansas City | Kansas City | United States | 3 |
| Cincinnati Children's Hospital Medical Center | Cincinnati | United States | 405 |
| Dana-Farber Cancer Institute (adult patients) | Boston | United States | 1 |
| Fred Hutch/University of Washington/Seattle Children's Cancer Consortium | Seattle | United States | 3 |
| Hackensack University Medical Center | Hackensack | United States | 308 |
| Karolinska University Hospital | Stockholm | Sweden | 87 |
| Massachusetts General Hospital | Boston | United States | 1015 |
| Oslo University Hospital | Oslo | Norway | 111 |
| University of Chicago | Chicago | United States | 312 |
| University of Wisconsin Hospital and Clinics | Madison | United States | 37 |