Wolfram syndrome
Wolfram syndrome
Explore linked clinical trials. Standard reference: MONDO:00181055 results · Page 1 of 1
Clinical trials
Swipe the table sideways for more columns.
| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| AMX0035 in Adult Patients With Wolfram Syndrome | Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Deaf-Blind Disorders, Deafness, Ear Diseases, Eye Diseases, Hereditary, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Neurologic Manifestations, Nutritional and Metabolic Diseases, Sensation Disorders, Urogenital Diseases, Wolfram syndrome, blindness (disorder), cranial nerve neuropathy, diabetes insipidus, diabetes mellitus, endocrine system disorder, eye disorder, glucose metabolism disease, hearing disorder, hearing loss disorder, hereditary disease, hereditary optic atrophy, inherited neurodegenerative disorder, kidney disorder, metabolic disease, nervous system disorder, neurodegenerative disease, optic atrophy, optic nerve disorder, otorhinolaryngologic disease, pituitary gland disorder, type 1 diabetes mellitus, urinary system disorder, vision disorder | Active, not recruiting | Phase 2 | 2026-04-14 | NCT05676034 | |
| Does Recessive Optic Atrophy Due to WFS1 Exist? | Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Deaf-Blind Disorders, Deafness, Ear Diseases, Eye Diseases, Hereditary, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Neurologic Manifestations, Nutritional and Metabolic Diseases, Sensation Disorders, Urogenital Diseases, Wolfram syndrome, Wolfram syndrome 1, blindness (disorder), cranial nerve neuropathy, diabetes insipidus, diabetes mellitus, endocrine system disorder, eye disorder, glucose metabolism disease, hearing disorder, hearing loss disorder, hereditary disease, hereditary optic atrophy, inherited neurodegenerative disorder, kidney disorder, metabolic disease, nervous system disorder, neurodegenerative disease, optic atrophy, optic nerve disorder, otorhinolaryngologic disease, pituitary gland disorder, type 1 diabetes mellitus, urinary system disorder, vision disorder | Not yet recruiting | Not stated | 2026-01-13 | NCT07336966 | |
| Mechanisms of Fecal Incontinence in Wolfram Syndrome | Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Deaf-Blind Disorders, Deafness, Digestive System Diseases, Ear Diseases, Eye Diseases, Hereditary, Fecal Incontinence, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Neurologic Manifestations, Nutritional and Metabolic Diseases, Sensation Disorders, Urogenital Diseases, Wolfram syndrome, blindness (disorder), cranial nerve neuropathy, diabetes insipidus, diabetes mellitus, digestive system disorder, endocrine system disorder, eye disorder, glucose metabolism disease, hearing disorder, hearing loss disorder, hereditary disease, hereditary optic atrophy, inherited neurodegenerative disorder, intestinal disorder, kidney disorder, metabolic disease, nervous system disorder, neurodegenerative disease, optic atrophy, optic nerve disorder, otorhinolaryngologic disease, pituitary gland disorder, rectal disorder, type 1 diabetes mellitus, urinary system disorder, vision disorder | Not yet recruiting | Not stated | 2025-12-31 | NCT07313085 | |
| Wolfram Syndrome and WFS1-related Disorders International Registry and Clinical Study | Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Deaf-Blind Disorders, Deafness, Dyskinesias, Ear Diseases, Eye Diseases, Hereditary, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Neurologic Manifestations, Nutritional and Metabolic Diseases, Pathological Conditions, Signs and Symptoms, Sensation Disorders, Signs and Symptoms, Urogenital Diseases, Wolfram syndrome, atactic disorder, non-human animal, blindness (disorder), cranial nerve neuropathy, diabetes insipidus, diabetes mellitus, endocrine system disorder, eye disorder, glucose metabolism disease, hearing disorder, hearing loss disorder, hereditary disease, hereditary optic atrophy, inherited neurodegenerative disorder, kidney disorder, metabolic disease, nervous system disorder, neurodegenerative disease, optic atrophy, optic nerve disorder, otorhinolaryngologic disease, pituitary gland disorder, type 1 diabetes mellitus, urinary system disorder, vision disorder | Recruiting | Not stated | 2025-12-23 | NCT02841553 | |
| Monogenic Diabetes Misdiagnosed as Type 1 | Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Deaf-Blind Disorders, Deafness, Ear Diseases, Eye Diseases, Hereditary, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Neurologic Manifestations, Nutritional and Metabolic Diseases, Sensation Disorders, Urogenital Diseases, Wolcott-Rallison syndrome, Wolfram syndrome, autoimmune disease, blindness (disorder), cranial nerve neuropathy, diabetes insipidus, diabetes mellitus, endocrine system disorder, eye disorder, glucose metabolism disease, hearing disorder, hearing loss disorder, hereditary disease, hereditary optic atrophy, immune system disorder, inherited neurodegenerative disorder, kidney disorder, maternally-inherited diabetes and deafness, metabolic disease, monogenic diabetes, nervous system disorder, neurodegenerative disease, optic atrophy, optic nerve disorder, otorhinolaryngologic disease, pituitary gland disorder, type 1 diabetes mellitus, urinary system disorder, vision disorder | Recruiting | Not stated | 2024-12-10 | NCT03988764 |