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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
AMX0035 in Adult Patients With Wolfram SyndromeAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Deaf-Blind Disorders, Deafness, Ear Diseases, Eye Diseases, Hereditary, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Neurologic Manifestations, Nutritional and Metabolic Diseases, Sensation Disorders, Urogenital Diseases, Wolfram syndrome, blindness (disorder), cranial nerve neuropathy, diabetes insipidus, diabetes mellitus, endocrine system disorder, eye disorder, glucose metabolism disease, hearing disorder, hearing loss disorder, hereditary disease, hereditary optic atrophy, inherited neurodegenerative disorder, kidney disorder, metabolic disease, nervous system disorder, neurodegenerative disease, optic atrophy, optic nerve disorder, otorhinolaryngologic disease, pituitary gland disorder, type 1 diabetes mellitus, urinary system disorder, vision disorderActive, not recruitingPhase 22026-04-14NCT05676034

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OrganizationsLinked trials
Amylyx Pharmaceuticals Inc.3

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Research sitesCityCountryLinked trials
Washington UniversitySt LouisUnited States182