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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
CS-121 APOC3 Base Editing in Severe HypertriglyceridemiaDyslipidemias, Lipid Metabolism Disorders, Nutritional and Metabolic Diseases, hyperlipidemia, hypertriglyceridemia, metabolic diseaseNot yet recruitingEarly phase 12026-06-18NCT07657780
CS-101 in Patients With β-thalassemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaEnrolling by invitationEarly phase 12026-06-09NCT06328764
A Phase 2 Safety and Efficacy Study Evaluating CS-101 in Participants With β-Thalassemia Majorβ-thalassemia MajorNot yet recruitingPhase 22026-03-24NCT07489196
CS-121 APOC3 Base Editing in FCSDigestive System Diseases, Dyslipidemias, Lipid Metabolism Disorders, Nutritional and Metabolic Diseases, familial lipoprotein lipase deficiency, hyperlipidemia, hypertriglyceridemia, metabolic disease, pancreas disorder, pancreatitisRecruitingEarly phase 12026-02-11NCT07176923
A Follow-up Study to Evaluate the Long-term Safety and Efficacy in Participants Who Received CS-101 InjectionCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaEnrolling by invitationNot stated2026-02-10NCT06717932
A Long-term Follow-up Study in Participants Who Received CS-101Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaEnrolling by invitationNot stated2026-02-10NCT06685536
CS-206 in Patients With Sickle Cell DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseRecruitingEarly phase 12026-02-10NCT06565026
CS-121 APOC3 Base Editing in Children and Adolescents With HyperchylomicronemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Dyslipidemias, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, familial lipoprotein lipase deficiency, hereditary disease, hyperlipidemia, hyperlipoproteinemia, inborn errors of metabolism, metabolic disease, pancreas disorder, pancreatitisRecruitingEarly phase 12026-01-28NCT07371767