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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, hereditary disease, inherited neurodegenerative disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myotonic dystrophy, myotonic dystrophy type 1, myotonic syndrome, nervous system disorder, neurodegenerative disease, neuromuscular diseaseRecruitingNot stated2026-06-10NCT03981575
ALS/MND Natural History Study Data RepositoryCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Kennedy disease, Nutritional and Metabolic Diseases, TDP-43 proteinopathy, X-linked disease, amyotrophic lateral sclerosis, central nervous system disorder, hereditary disease, inherited neurodegenerative disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, progressive bulbar palsy, proteostasis deficiencies, spinal cord disorder, spinal muscular atrophyRecruitingNot stated2026-05-20NCT05966038
Transition to Adulthood in People With Muscular DystrophyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseNot yet recruitingNot applicable2025-08-03NCT07101185