Elpida Therapeutics SPC
Elpida Therapeutics SPC
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Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Study of Intrathecal ELP-02 for Charcot-Marie-Tooth Disease Type 4J (CMT4J) | Charcot-Marie-Tooth disease type 4J | Recruiting | Phase 1 / Phase 2 | 2026-09-09 | NCT07447557 | |
| A Prospective Natural History and Outcome Measure Discovery Study of Charcot-Marie-Tooth Disease, Type 4J | nervous system disorder, neuromuscular disease, peripheral nervous system disorder | Active, not recruiting | Not stated | 2026-07-08 | NCT06151600 | |
| Melpida: Recombinant Adeno-associated Virus (Serotype 9) Encoding a Codon Optimized Human AP4M1 Transgene (hAP4M1opt) | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Malformations of Cortical Development, Group I, Muscle Hypertonia, Muscle Spasticity, Musculoskeletal Abnormalities, Neurologic Manifestations, Neuromuscular Manifestations, Paraplegia, Spastic, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, central nervous system malformation, cerebral cortical dysplasia, hereditary spastic paraplegia 50, microcephaly, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, palsy, paraplegia | Recruiting | Phase 1 / Phase 2 | 2026-07-08 | NCT05518188 | |
| Phase 3 Efficacy Study With Concurrent Control of IT MELPIDA in SPG50.Concurrent Controls. | Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, hereditary spastic paraplegia 50, nervous system disorder, palsy, paraplegia | Recruiting | Phase 3 | 2026-04-20 | NCT06692712 | |
| A Safety and Efficacy of Intrathecally Administered ION283 in Patients With Lafora Disease | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Epilepsies, Myoclonic, Epilepsy, Generalized, Epileptic Syndromes, Lafora disease, brain disorder, central nervous system disorder, epilepsy, hereditary disease, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, progressive myoclonus epilepsy | Recruiting | Phase 1 / Phase 2 | 2025-12-18 | NCT06609889 |