Melpida: Recombinant Adeno-associated Virus (Serotype 9) Encoding a Codon Optimized Human AP4M1 Transgene (hAP4M1opt) | ClinicalTrials HQ

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Trial	Conditions	Status	Phase	Updated	More info	NCT ID
Melpida: Recombinant Adeno-associated Virus (Serotype 9) Encoding a Codon Optimized Human AP4M1 Transgene (hAP4M1opt)	Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Malformations of Cortical Development, Group I, Muscle Hypertonia, Muscle Spasticity, Musculoskeletal Abnormalities, Neurologic Manifestations, Neuromuscular Manifestations, Paraplegia, Spastic, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, central nervous system malformation, cerebral cortical dysplasia, hereditary spastic paraplegia 50, microcephaly, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, palsy, paraplegia	Recruiting	Phase 1 / Phase 2	2026-07-08		NCT05518188

2 results · Page 1 of 1

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Organizations	Linked trials
Elpida Therapeutics SPC	5
University of Texas Southwestern Medical Center	295

1 results · Page 1 of 1

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Research sites	City	Country	Linked trials
Children's Medical Center Dallas	Dallas	United States	18