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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Urogenital Abnormalities, Urogenital Diseases, adrenal gland disorder, adrenogenital syndrome, congenital adrenal hyperplasia, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, hereditary disease, inborn errors of metabolism, metabolic disease, steroid inherited metabolic disorderActive, not recruitingPhase 1 / Phase 22025-12-23NCT04783181