A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)
A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)
Active, not recruiting · NCT04783181 · Registry updated 2025-12-23Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH) | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Urogenital Abnormalities, Urogenital Diseases, adrenal gland disorder, adrenogenital syndrome, congenital adrenal hyperplasia, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, hereditary disease, inborn errors of metabolism, metabolic disease, steroid inherited metabolic disorder | Active, not recruiting | Phase 1 / Phase 2 | 2025-12-23 | NCT04783181 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Adrenas Therapeutics Inc | 1 |
5 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Ann and Robert H. Lurie Children's Hospital of Chicago | Chicago | United States | 14 |
| Children's Hospital of Philadelphia | Philadelphia | United States | 434 |
| Lucas Research, Inc. | Morehead City | United States | 7 |
| National Institutes of Health Clinical Center | Bethesda | United States | 1 |
| University of Minnesota | Minneapolis | United States | 325 |