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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Safety, Tolerability and Efficacy of ICV AX 250 Treatment in MPS IIIB -OLECongenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 3BEnrolling by invitationPhase 42023-08-09NCT05492799