Safety, Tolerability and Efficacy of ICV AX 250 Treatment in MPS IIIB -OLE
Safety, Tolerability and Efficacy of ICV AX 250 Treatment in MPS IIIB -OLE
Enrolling by invitation · NCT05492799 · Registry updated 2023-08-09Clinical trials
Swipe the table sideways for more columns.
| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Safety, Tolerability and Efficacy of ICV AX 250 Treatment in MPS IIIB -OLE | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 3B | Enrolling by invitation | Phase 4 | 2023-08-09 | NCT05492799 |
1 results · Page 1 of 1
Organizations
Swipe the table sideways for more columns.
| Organizations | Linked trials |
|---|---|
| Allievex Corporation | 1 |
6 results · Page 1 of 1
Research sites
Swipe the table sideways for more columns.
| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Fundación Cardio Infantil - Instituto de Cardiología | Bogotá | Colombia | 2 |
| Gazi University Faculty of Medicine | Ankara | Turkey (Türkiye) | 4 |
| Great Ormond Street Hospital For Children, NHS Foundation Trust | London | United Kingdom | 1 |
| UCSF Benioff Children's Hospital Oakland | Oakland | United States | 85 |
| University Medical Center Hamburg-Eppendorf | Hamburg | Germany | 24 |
| UPMC Children's Hospital Pittburgh | Pittsburgh | United States | 1 |