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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMITCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingNot stated2026-09-24NCT06564974
I-DECIDE After Bronchiolitis HospitalizationBronchiolitis AcuteRecruitingNot applicable2026-09-10NCT07243652
Pediatric Influence of Cooling Duration on Efficacy in Cardiac Arrest Patients (P-ICECAP)Body Temperature Changes, Coma, Consciousness Disorders, Hypothermia, Hypoxia, Hypoxia, Brain, Neurobehavioral Manifestations, Neurologic Manifestations, Out-of-Hospital Cardiac Arrest, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Signs and Symptoms, Respiratory, Unconsciousness, brain disorder, brain hypoxia - ischemia, brain ischemia, cardiac arrest, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, heart disorder, nervous system disorder, vascular disorderRecruitingNot applicable2026-09-08NCT05376267
A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular DystrophyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 32026-08-28NCT05126758
A Study to Learn About Medicine Called Ritlecitinib in Children Aged Between 6 to 12 Years With Severe Alopecia AreataSkin and Connective Tissue Diseases, alopecia, alopecia areata, disorder of pilosebaceous unit, hypotrichosis, skin disorderActive, not recruitingPhase 32026-08-26NCT07029711
A Study to Evaluate the Effect of Aficamten in Pediatric Patients With Symptomatic Obstructive Hypertrophic Cardiomyopathy (oHCM).Pediatric; Symptomatic Obstructive Hypertrophic CardiomyopathyActive, not recruitingPhase 2 / Phase 32026-08-18NCT06412666
Pediatric cGVHD Symptom Scalegraft versus host disease, immune system disorderActive, not recruitingNot stated2026-08-10NCT04044365
ARDS in Children and ECMO Initiation Strategies Impact on Neurodevelopment (ASCEND)Respiration Disorders, adult acute respiratory distress syndrome, lung disorder, respiratory system disorderActive, not recruitingNot stated2026-07-14NCT05388708
Rethinking Early Airway Clearence TherapiesCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderNot yet recruitingNot applicable2026-07-10NCT07696338
Morphine or Ketamine for AnalgesiaAbdominal Pain, Disease Attributes, Emergencies, Neurobehavioral Manifestations, Neurologic Manifestations, Pain, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Signs and Symptoms, Digestive, agnosia, anxiety disorder, bone fracture, depressive disorder, injury, nervous system disorder, perceptual disorders, psychiatric disorderNot yet recruitingPhase 32026-06-09NCT06835504
Retinoblastoma Phase II Expanded Access Clinical TrialEye Diseases, Hereditary, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, epithelial neoplasm, eye disorder, neoplasm, neuroepithelial neoplasm, ocular cancer, primitive neuroectodermal tumor, retinal cancer, retinal disorder, retinoblastomaRecruitingPhase 22026-05-22NCT06679634
MCW Alpha/Beta T-Cell and B-Cell Depletion With Targeted ATG DosingB-cell neoplasm, Burkitt Leukemia, Burkitt lymphoma, Chronic Disease, DNA Virus Infections, Disease Attributes, Epstein-Barr virus infection, Hemic and Lymphatic Diseases, Herpesviridae infectious disease, Infections, Leukemia, Myelogenous, Chronic, BCR-ABL Positive, Leukemia, Myeloid, Chronic-Phase, Myeloproliferative Disorders, Neoplasms by Histologic Type, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Tumor Virus Infections, acute biphenotypic leukemia, anemia, bone marrow disorder, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, leukemia, myeloid, accelerated-phase, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, myelodysplastic syndrome, myelodysplastic syndrome with excess blasts, myelodysplastic syndrome with single lineage dysplasia, myeloid leukemia, neoplasm, viral infectious diseaseRecruitingNot applicable2026-05-13NCT05794880
A Study of Auricular Neurostimulation for Children With Cyclic Vomiting SyndromeFamilial cyclic vomiting syndromeRecruitingNot applicable2026-03-16NCT07465614
Supraglottic Airway for Resuscitation TrialDelivery Room Resuscitation; Implementation Research; Infant, Newborn; Laryngeal Mask Airways; Neonatal Resuscitation; Positive Pressure Ventilation; Supraglottic AirwayRecruitingNot applicable2026-02-27NCT07150923
Eliminating Monitor Overuse Trial (EMO Trial)Bronchiolitis Acute ViralActive, not recruitingNot applicable2026-02-13NCT05132322
Metformin for Premature Infants With Bronchopulmonary DysplasiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases and Pregnancy Complications, Infant, Newborn, Diseases, Infant, Premature, Diseases, Lung Injury, Obstetric Labor Complications, Obstetric Labor, Premature, Premature Birth, Urogenital Diseases, Ventilator-Induced Lung Injury, bronchopulmonary dysplasia, lung disorder, pregnancy disorder, respiratory system disorderRecruitingEarly phase 12026-01-26NCT07120971
PTGS1 Genetic Variation and Increased Risk for Persistent Pulmonary Hypertension of the NewbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Infant, Newborn, Diseases, lung disorder, persistent fetal circulation syndrome, pulmonary hypertension, respiratory system disorderRecruitingNot stated2026-01-26NCT00710177
Genetic Variants and Susceptibility to Diseases of Prematurity in Very Low Birth-Weight InfantsChronic Lung DiseaseRecruitingNot stated2026-01-26NCT00710112
Venetoclax to Augment Epigenetic Modification and ChemotherapyHemic and Lymphatic Diseases, Neoplasms by Histologic Type, acute myeloid leukemia, hematologic disorder, leukemia, myeloid leukemia, neoplasmRecruitingPhase 12026-01-12NCT05317403
Optimal Ventilation for Cardiac Arrestcardiac arrest, cardiovascular disorder, heart disorderRecruitingNot applicable2025-10-08NCT07114510
Screen Smart: Using Digital Health to Improve HIV Screening and PreventionBlood-Borne Infections, Disease Attributes, Emergencies, Genital Diseases, HIV infectious disease, Infections, Pathologic Processes, Pathological Conditions, Signs and Symptoms, RNA Virus Infections, Urogenital Diseases, immune system disorder, inborn error of immunity, infectious disease, lentivirus infection, sexually transmitted disease, uterine carcinosarcoma, viral infectious disease, viral sexually transmitted diseaseRecruitingNot applicable2025-05-04NCT06003192
Percutaneous Intervention Versus Observational Trial of Arterial Ductus in Low Weight InfantsCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorder, patent ductus arteriosusRecruitingNot applicable2025-03-30NCT05547165
Sickle Cell Improvement: Enhancing Care in the Emergency DepartmentCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Vaso-Occlusive Crises, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseRecruitingNot applicable2023-08-14NCT05373771