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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMITCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingNot stated2026-09-24NCT06564974

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Research sitesCityCountryLinked trials
Arkansas Childrens HospitalLittle RockUnited States4
Atrium Health Neurosciences InstituteCharlotteUnited States2
Children's Hospital Los AngelesLos AngelesUnited States226
Children's Hospital of Philadelphia (CHOP)PhiladelphiaUnited States7
Children's National Health SystemWashington D.C.United States19
Children's WisconsinMilwaukeeUnited States23
Cincinnati Children's Hospital Medical CenterCincinnatiUnited States405
Duke University Medical Center and Childrens Health CenterDurhamUnited States1
FDI Clinical ResearchSan JuanPuerto Rico1
Helen DeVos Children's HospitalGrand RapidsUnited States23
Indiana University Health - Riley Hospital for ChildrenIndianapolisUnited States1
Johns Hopkins All Children's HospitalSt. PetersburgUnited States116
Loma Linda University Pediatric Subspecialty ClinicsLoma LindaUnited States1
Lurie Children's Hospital of ChicagoChicagoUnited States16
Masonic Children's Hospital - Discovery ClinicMinneapolisUnited States1
Nemours Children's HospitalOrlandoUnited States84
Neurology Rare Disease Center - Neurology & Neuromuscular Care CenterDentonUnited States1
Nicklaus Children's HospitalMiamiUnited States112
Penn State Milton S. Hershey Medical Center- Penn State Hershey Neuroscience InstituteHersheyUnited States1
Phoenix Children's HospitalPhoenixUnited States95
San Jorge Children's HospitalSan JuanPuerto Rico1
Seattle Children's HospitalSeattleUnited States281
Stanford UniversityPalo AltoUnited States51
The Children's Hospital at MontefioreThe BronxUnited States1
The University of Texas Health Science Center at San AntonioSan AntonioUnited States26