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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
REVEAL: A Phase 3 Study of Obudanersen (ION582) in Angelman SyndromeAbnormalities, Multiple, Angelman syndrome, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Imprinting Disorders, central nervous system disorder, chromosomal disorder, hereditary disease, movement disorder, nervous system disorderActive, not recruitingPhase 32026-09-29NCT06914609
ECMO ABI Detection With HyperfineCraniocerebral Trauma, Hypoxia, Hypoxia, Brain, Injuries, Acute Brain, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Signs and Symptoms, Respiratory, Stroke, Acute, brain disorder, brain hypoxia - ischemia, brain injury, brain ischemia, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, injury, nervous system disorder, nervous system injury, stroke disorder, vascular disorderRecruitingNot applicable2026-09-24NCT06469801
Campath/Fludarabine/Melphalan Transplant Conditioning for Non-Malignant DiseasesCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, hematologic disorder, hereditary disease, inherited hemoglobinopathy, metabolic diseaseRecruitingPhase 1 / Phase 22026-09-16NCT00920972
Regulating Together for Intellectual Disability and Autism: A Group Behavioral Therapy for for Emotion DysregulationNeurobehavioral Manifestations, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, autism, autism spectrum disorder, intellectual disability, nervous system disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorderRecruitingNot applicable2026-09-03NCT07624448
Regulating Together for Prader-Willi Syndrome: A Group Behavioral Therapy for Emotion DysregulationAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hyperphagia, Imprinting Disorders, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Overweight, Pathological Conditions, Signs and Symptoms, Prader-Willi syndrome, Signs and Symptoms, Signs and Symptoms, Digestive, anxiety disorder, chromosomal disorder, depressive disorder, hereditary disease, intellectual disability, nervous system disorder, nutritional disorder, obesity disorder, overnutrition, psychiatric disorderRecruitingNot applicable2026-09-02NCT07607730
Phase 3 Efficacy and Safety Study of GTX-102 in Pediatric Subjects With Angelman Syndrome (AS)Abnormalities, Multiple, Angelman syndrome, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Imprinting Disorders, central nervous system disorder, chromosomal disorder, hereditary disease, movement disorder, nervous system disorderActive, not recruitingPhase 32026-08-06NCT06617429
ARDS in Children and ECMO Initiation Strategies Impact on Neurodevelopment (ASCEND)Respiration Disorders, adult acute respiratory distress syndrome, lung disorder, respiratory system disorderActive, not recruitingNot stated2026-07-14NCT05388708
A Feasibility Trial of Virtual Reality Neurofeedback for Adolescents With Migrainebrain disorder, central nervous system disorder, headache disorder, hypnic headache, migraine disorder, nervous system disorderRecruitingNot applicable2026-06-03NCT07454798
Heavy Menstrual Bleeding Progestin Treatment in Bleeding Disorders StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Hemic and Lymphatic Diseases, Hemorrhage, Menorrhagia, Menstruation Disturbances, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, Uterine Hemorrhage, blood coagulation disease, blood platelet disease, cardiovascular disorder, coagulation protein disease, female reproductive system disorder, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, uterine disorder, vascular disorder, vascular hemostatic disease, von Willebrand disease (hereditary or acquired)RecruitingNot stated2025-12-17NCT05916469
Non-Invasive Diagnosis of Pediatric Pulmonary Invasive Mold InfectionsBacterial Infections and Mycoses, Infections, Invasive Fungal Infections, Invasive Pulmonary Aspergillosis, aspergillosis, fungal infectious disease, fungal lung infectious disease, lung disorder, pulmonary aspergilloma, respiratory system disorderRecruitingNot stated2024-09-25NCT03827694