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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Phase 3 Efficacy and Safety Study of GTX-102 in Pediatric Subjects With Angelman Syndrome (AS)Abnormalities, Multiple, Angelman syndrome, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Imprinting Disorders, central nervous system disorder, chromosomal disorder, hereditary disease, movement disorder, nervous system disorderActive, not recruitingPhase 32026-08-06NCT06617429

1 results · Page 1 of 1

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OrganizationsLinked trials
Ultragenyx Pharmaceutical Inc24

28 results · Page 1 of 2

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Research sitesCityCountryLinked trials
Boston Children's HospitalBostonUnited States343
British Columbia Children's HospitalVancouverCanada3
Carum Research IncDallasUnited States1
Cedars SinaiLos AngelesUnited States21
Children's Hospital ColoradoAuroraUnited States312
Children's MercyKansas CityUnited States10
Columbia University Medical centerNew YorkUnited States224
Haunersche KinderklinikMunichGermany1
Hokkaido University HospitalSapporoJapan34
Hospital Sant Joan de DeuBarcelonaSpain11
Hospital Universitario Parc TauliBarcelonaSpain1
Hospital Universitario Puerta de HierroMadridSpain12
Hospital Universitario Virgen Del RocioSevilleSpain186
McGill University Health CentreMontrealCanada10
Medical University of GdańskGdanskPoland1
Nagoya City University Graduate School of Medical SciencesNagoyaJapan1
Nicklaus Children's HospitalMiamiUnited States112
Osaka City General HospitalOsakaJapan1
Polish Mothers Memorial InstituteLodzPoland1
Rare Disease ResearchHillsboroughUnited States4
Rare Disease ResearchAtlantaUnited States12
Rush UniversityChicagoUnited States36
The University of TexasAustinUnited States1
UCSD, Rady Children's HospitalSan DiegoUnited States1
UCSFSan FranciscoUnited States27