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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Pegtibatinase as a Treatment for Participants With Classical Homocystinuria (HCU) Receiving Standard of Care TreatmentBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, brain disorder, central nervous system disorder, connective tissue disorder, hereditary disease, homocystinuria, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorderRecruitingPhase 32026-10-08NCT06247085
Postoperative Acute Kidney Injury in Children Undergoing Major Non-cardiac SurgeryFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Urogenital Diseases, acute kidney injury, kidney disorder, kidney failure, urinary system disorderRecruitingNot stated2026-09-29NCT07351149
A Long-term Extension Study to Assess the Long-term Safety and Efficacy of Pegtibatinase Treatment in Participants ≥5 to ≤65 Years of Age With Classical Homocystinuria (HCU) (ENSEMBLE)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, brain disorder, central nervous system disorder, connective tissue disorder, hereditary disease, homocystinuria, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorderEnrolling by invitationPhase 32026-05-28NCT06431893
SLIT ABS: Study on Patients With Autoimmune PodocytopathyFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nephrotic Syndrome, Minimal Change, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, disease, focal segmental glomerulosclerosis, glomerulonephritis, kidney disorder, minimal change disease, nephritis, nephrosis, urinary system disorderRecruitingNot applicable2026-04-08NCT07516964
Lung Ultrasound for Guiding Antibiotic Use in Pediatric PneumoniaInfections, lung disorder, pneumonia, respiratory system disorder, respiratory tract infectious disorderRecruitingNot applicable2026-04-03NCT06921993
National Multicentre Study on Lipid Profile in Noonan Syndrome and Related Disorders: Trends by Age, Gender and GenotypeCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Musculoskeletal Abnormalities, Noonan syndrome, Skin and Connective Tissue Diseases, cardiovascular disorder, congenital heart disease, connective tissue disorder, heart disorder, musculoskeletal system disorderRecruitingNot stated2026-03-11NCT07464821
European and North Indian Cohort of KaWasaki dIseaseHemic and Lymphatic Diseases, Kawasaki disease, Skin and Connective Tissue Diseases, cardiovascular disorder, lymphatic system disorder, skin disorder, skin vascular disease, vascular disorder, vasculitisRecruitingNot stated2025-09-29NCT06305611
Multicenter Italian Cohort Study on Tuberculosis in Pediatric AgeActinomycetales infectious disease, Bacterial Infections and Mycoses, Infections, bacterial infectious disease, disease arising from reactivation of latent virus, gram-positive bacterial infections, latent tuberculosis infection, mycobacterial infectious disease, tuberculosisRecruitingNot stated2024-03-04NCT06289660