IRCCS Istituto Giannina Gaslini
IRCCS Istituto Giannina Gaslini
Genova, Italy8 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Pegtibatinase as a Treatment for Participants With Classical Homocystinuria (HCU) Receiving Standard of Care Treatment | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, brain disorder, central nervous system disorder, connective tissue disorder, hereditary disease, homocystinuria, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder | Recruiting | Phase 3 | 2026-10-08 | NCT06247085 | |
| Postoperative Acute Kidney Injury in Children Undergoing Major Non-cardiac Surgery | Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Urogenital Diseases, acute kidney injury, kidney disorder, kidney failure, urinary system disorder | Recruiting | Not stated | 2026-09-29 | NCT07351149 | |
| A Long-term Extension Study to Assess the Long-term Safety and Efficacy of Pegtibatinase Treatment in Participants ≥5 to ≤65 Years of Age With Classical Homocystinuria (HCU) (ENSEMBLE) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, brain disorder, central nervous system disorder, connective tissue disorder, hereditary disease, homocystinuria, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder | Enrolling by invitation | Phase 3 | 2026-05-28 | NCT06431893 | |
| SLIT ABS: Study on Patients With Autoimmune Podocytopathy | Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nephrotic Syndrome, Minimal Change, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, disease, focal segmental glomerulosclerosis, glomerulonephritis, kidney disorder, minimal change disease, nephritis, nephrosis, urinary system disorder | Recruiting | Not applicable | 2026-04-08 | NCT07516964 | |
| Lung Ultrasound for Guiding Antibiotic Use in Pediatric Pneumonia | Infections, lung disorder, pneumonia, respiratory system disorder, respiratory tract infectious disorder | Recruiting | Not applicable | 2026-04-03 | NCT06921993 | |
| National Multicentre Study on Lipid Profile in Noonan Syndrome and Related Disorders: Trends by Age, Gender and Genotype | Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Musculoskeletal Abnormalities, Noonan syndrome, Skin and Connective Tissue Diseases, cardiovascular disorder, congenital heart disease, connective tissue disorder, heart disorder, musculoskeletal system disorder | Recruiting | Not stated | 2026-03-11 | NCT07464821 | |
| European and North Indian Cohort of KaWasaki dIsease | Hemic and Lymphatic Diseases, Kawasaki disease, Skin and Connective Tissue Diseases, cardiovascular disorder, lymphatic system disorder, skin disorder, skin vascular disease, vascular disorder, vasculitis | Recruiting | Not stated | 2025-09-29 | NCT06305611 | |
| Multicenter Italian Cohort Study on Tuberculosis in Pediatric Age | Actinomycetales infectious disease, Bacterial Infections and Mycoses, Infections, bacterial infectious disease, disease arising from reactivation of latent virus, gram-positive bacterial infections, latent tuberculosis infection, mycobacterial infectious disease, tuberculosis | Recruiting | Not stated | 2024-03-04 | NCT06289660 |