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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Pegtibatinase as a Treatment for Participants With Classical Homocystinuria (HCU) Receiving Standard of Care TreatmentBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, brain disorder, central nervous system disorder, connective tissue disorder, hereditary disease, homocystinuria, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorderRecruitingPhase 32026-10-08NCT06247085

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OrganizationsLinked trials
Travere Therapeutics, Inc.10

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Research sitesCityCountryLinked trials
Ann & Robert H. Lurie Children's Hospital of ChicagoChicagoUnited States144
Assistance Publique - Hôpitaux de Paris (AP-HP) - Hôpital Necker-Enfants MaladesParisFrance2
Azienda Ospedaliera di PadovaPadovaItaly15
Birmingham Women's and Children's NHS Foundation TrustBirminghamUnited Kingdom7
Centre Hospitalier Régional Universitaire de Nancy (CHRU) - Hopitaux de Brabois - Hôpital d'enfantsVandœuvre-lès-NancyFrance2
Children's Health Ireland (CHI) at Temple StreetDublinIreland2
Children's Hospital of PhiladelphiaPhiladelphiaUnited States434
CHRU Hôpitaux de Tours - Hôpital BretonneauToursFrance2
Cliniques universitaires Saint-LucBrusselsBelgium37
Complejo Hospitalario Universitario de Santiago (CHUS) - Hospital Clínico UniversitarioSantiago de CompostelaSpain2
Ege Üniversitesi Hastanesi BornovaBornovaTurkey (Türkiye)2
Emory UniversityAtlantaUnited States262
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico (Policlinico di Milano)MilanItaly2
Fondazione IRCCS San Gerardo Dei Tintori - Ospedale San GerardoMonzaItaly2
Gazi University HospitalAnkaraTurkey (Türkiye)4
Hamad General HospitalDohaQatar3
Hospital Sant Joan de DéuBarcelonaSpain11
Hospital Universitario 12 De OctubreMadridSpain98
Hospital Universitario Ramón y CajalMadridSpain42
Hospital Universitario Virgen del RocíoSevilleSpain37
Instytut Matki i DzieckaWarsawPoland3
Instytut Pomnik-Centrum Zdrowia DzieckaWarsawPoland3
IRCCS Istituto Giannina GasliniGenovaItaly8
Istanbul University Cerrahpasa HospitalIstanbulTurkey (Türkiye)2
King Abdullah International Medical Research CenterRiyadhSaudi Arabia2