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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
DFT383 in Pediatric Participants With Nephropathic CystinosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Fanconi renotubular syndrome, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Urogenital Diseases, cystinosis, hereditary disease, inborn errors of metabolism, kidney disorder, lysosomal storage disease, metabolic disease, nephropathic cystinosis, renal tubular transport disease, urinary system disorderRecruitingPhase 1 / Phase 22026-09-22NCT06910813