DFT383 in Pediatric Participants With Nephropathic Cystinosis
DFT383 in Pediatric Participants With Nephropathic Cystinosis
Recruiting · NCT06910813 · Registry updated 2026-09-22Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| DFT383 in Pediatric Participants With Nephropathic Cystinosis | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fanconi renotubular syndrome, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Urogenital Diseases, cystinosis, hereditary disease, inborn errors of metabolism, kidney disorder, lysosomal storage disease, metabolic disease, nephropathic cystinosis, renal tubular transport disease, urinary system disorder | Recruiting | Phase 1 / Phase 2 | 2026-09-22 | NCT06910813 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Novartis Pharmaceuticals | 432 |
6 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Baylor College of Medicine - Texas Children's Hospital (recuiting Cohort 0) | Houston | United States | 1 |
| Children's Hospital of Philadelphia (Recruiting Cohort 0 and 1) | Philadelphia | United States | 1 |
| Emory University School of Medicine - Children's Healthcare of Atlanta (recuiting Cohort 0) | Atlanta | United States | 1 |
| Phoenix Children's Hospital (Recruiting Cohort 0 and 1) | Phoenix | United States | 1 |
| Stanford University - Stanford Children's Health (Recruiting Cohort 0 and 1) | Stanford | United States | 1 |
| University of California at San Diego - Rady Children's Hospital (Recruiting Cohort 0 and 1) | San Diego | United States | 1 |