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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia BCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, X-linked disease, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderRecruitingPhase 1 / Phase 22026-10-08NCT06379789
Modification of Coronary Calcium With Laser Based Intravascular Lithotripsy for Coronary Artery Disease (FRACTURE)Arterial Occlusive Diseases, arteriosclerosis disorder, cardiovascular disorder, coronary artery disorder, heart disorder, myocardial ischemia, vascular disorderActive, not recruitingNot applicable2026-10-07NCT06181240
Comparing the Effects of Newer Pacemakers and Their Effects on the Heart and Valve Function in the Short-term.Ventricular Dysfunction, Ventricular Dysfunction, Right, cardiovascular disorder, heart disorder, heart valve disorder, tricuspid valve insufficiencyRecruitingNot stated2026-08-21NCT07534917
A Trial That Evaluates Disease Characteristics in Hemophilia B Adult Male Participants Receiving Prophylaxis With Standard of Care Factor IX Protein (FIX) Replacement TherapyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, X-linked disease, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderActive, not recruitingNot stated2026-08-07NCT05568459
RECANA OUS - Recana Thrombectomy Catheter System for Venous Obstruction and Occlusion Study (RECANA-OUS-UK)Embolism and Thrombosis, Postthrombotic Syndrome, Venous Thrombosis, cardiovascular disorder, thrombotic disease, vascular disorder, venous insufficiencyRecruitingNot applicable2026-05-06NCT07219758
Exploring the Cutaneous Immune Response to Skin Massage in Early LifeSkin MassageRecruitingNot applicable2026-02-11NCT07228728
Extension Study of Infigratinib in Children With Achondroplasia (ACH)Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, achondroplasia, bone disorder, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasiaEnrolling by invitationPhase 22025-10-31NCT05145010