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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia BCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, X-linked disease, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderRecruitingPhase 1 / Phase 22026-10-08NCT06379789

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Research sitesCityCountryLinked trials
Addenbrooke's Hospital, Cambridge University Hospitals NHS FTCambridgeUnited Kingdom2
Alfred HospitalMelbourneAustralia30
Careggi University HospitalFlorenceItaly2
Centro Estadual de Hemoterapia e Hematologia Marcos Daniel SantosVitóriaBrazil1
Children's Hospital Los AngelesLos AngelesUnited States226
Children's Hospital of Philadelphia (CHOP)PhiladelphiaUnited States7
Complejo Hospitalario Universitario de A Coruña (Edificio Teresa Herrera-Materno Infantil)A CoruñaSpain1
David Geffen School of Medicine at UCLALos AngelesUnited States2
Fondazione Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) Ca Granda Ospedale Maggiore PoliclinicoMilanItaly1
Glasgow Royal Infirmary - Clinical Research FacilityGlasgowUnited Kingdom1
Haemostasis and Thrombosis Unit, Hospital La FeValenciaSpain1
Hammersmith Hospital Comprehensive Care CentreLondonUnited Kingdom1
Hemocentro UnicampCampinasBrazil1
HemorioRio de JaneiroBrazil1
Hemostase Clinique, Institut Coeur PoumonLilleFrance1
Hopital NeckerParisFrance5
Hospices Civils de LyonBronFrance1
Hospital Clinico Universitario Virgen De La ArrixacaEl PalmarSpain10
Hospital Universitario Central de AsturiasOviedoSpain57
Hospital Universitario La PazMadridSpain217
Hospital Universitario Miguel ServetZaragozaSpain92
Hospital Universitario Vall D'HebronBarcelonaSpain86
Hospital Universitario Virgen del RocioSevilleSpain21
Indiana Hemophilia and Thrombosis CenterIndianapolisUnited States4
Irccs Humanitas Research HospitalRozzanoItaly1