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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorderRecruitingPhase 22026-06-23NCT07123155
Study of SGR-1505 in Mature B-Cell NeoplasmsALK-positive large B-cell lymphoma, B-cell chronic lymphocytic leukemia, B-cell neoplasm, Blood Protein Disorders, Burkitt lymphoma, Chronic Disease, DNA Virus Infections, Digestive System Diseases, Disease Attributes, Epstein-Barr virus infection, Hemic and Lymphatic Diseases, Herpesviridae infectious disease, Infections, Leukemia, B-Cell, Lymphoma, B-Cell, Marginal Zone, Neoplasms by Histologic Type, Pathologic Processes, Pathological Conditions, Signs and Symptoms, T-cell/histiocyte rich large B cell lymphoma, Tumor Virus Infections, Waldenstrom macroglobulinemia, cardiovascular disorder, diffuse large B-cell lymphoma, digestive system disorder, follicular lymphoma, hematologic disorder, hemorrhagic disease, high grade B-cell lymphoma, hypertrophic pyloric stenosis, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoplasmacytic lymphoma, lymphoproliferative syndrome, mantle cell lymphoma, monoclonal gammopathy, neoplasm, neoplasm of mature B-cells, nodal marginal zone B-cell lymphoma, non-Hodgkin lymphoma, plasma cell neoplasm, plasmablastic lymphoma, primary cutaneous follicle center lymphoma, primary effusion lymphoma, pyloric stenosis, splenic marginal zone lymphoma, stomach disorder, vascular disorder, vascular hemostatic disease, viral infectious diseaseRecruitingPhase 12026-02-13NCT05544019
Phase 3, Double-blind, Randomized, Placebo-controlled Trial to Evaluate the Efficacy and Safety of AR1001 in Participants With Early Alzheimer's Disease (Polaris-AD)Alzheimer disease, brain disorder, central nervous system disorder, cognitive disorder, dementia, nervous system disorder, neurodegenerative disease, psychiatric disorder, tauopathyActive, not recruitingPhase 32025-10-02NCT05531526