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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorderRecruitingPhase 22026-06-23NCT07123155

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OrganizationsLinked trials
Shionogi14

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Research sitesCityCountryLinked trials
A.O.U. Policlinico "G. Martino"MessinaItaly2
Aarhus University HospitalAarhusDenmark77
AOU Citta della Salute e della Scienza di Torino - Ospedale le MolinetteTorinoItaly3
AP-HP Hopital Raymond PoincareGarchesFrance1
Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La TimoneMarseilleFrance2
CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies NeuromusculairesNiceFrance2
Cincinnati Children's Hospital Medical CenterCincinnatiUnited States405
Duke University Medical CenterDurhamUnited States505
Emory University HospitalAtlantaUnited States131
Erasmus MCGE RotterdamNetherlands1
HLC Hopital Pierre WertheimerBronFrance1
Hospital Universitari i Politecnic La FeValenciaSpain14
Hospital Universitario 12 De OctubreMadridSpain98
Klinikum der Ludwig-Maximilians-Universitaet MuenchenMünchenGermany3
Lysosomal and Rare Disorders Research and Treatment Center (LDRTC)FairfaxUnited States2
National Hospital for Neurology & NeurosurgeryLondonUnited Kingdom3
Queen Elizabeth Hospital BirminghamBirminghamUnited Kingdom10
Royal Free London NHS Foundation TrustLondonUnited Kingdom15
Royal Victoria InfirmaryNewcastle upon TyneUnited Kingdom10
Salford Royal HospitalSalfordUnited Kingdom6
SphinCS GmbHHöchheimGermany2
Universitaetsklinikum Halle (Saale)HalleGermany1
University of California - Irvine Medical CenterIrvineUnited States2
University of Florida (UF) - GainesvilleGainesvilleUnited States1
University of PennsylvaniaPhiladelphiaUnited States507