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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study to Evaluate the Safety and Efficacy of Larsucosterol in Participants With Alcohol-associated Hepatitis (AH)Chemically-Induced Disorders, Digestive System Diseases, alcohol-induced disorders, alcohol-related disorders, alcoholic hepatitis, alcoholic liver disease, hepatitis, liver disorder, substance-related disorderRecruitingPhase 32026-10-06NCT07428538
A Randomized Multicenter Study for Isolated Skin VasculitisHemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Skin Manifestations, Skin and Connective Tissue Diseases, blood coagulation disease, cardiovascular disorder, cutaneous polyarteritis nodosa, hematologic disorder, hemorrhagic disease, immune system disorder, immunoglobulin A vasculitis, purpura, skin disorder, skin vascular disease, type III hypersensitivity disease, vascular disorder, vascular hemostatic disease, vasculitisRecruitingPhase 22026-08-20NCT02939573
Alpha-1 Antitrypsin Deficiency Adult Liver StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Fibrosis, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Subcutaneous Emphysema, alpha 1-antitrypsin deficiency, hereditary disease, liver disorder, lung disorder, pulmonary emphysema, respiratory system disorderActive, not recruitingNot stated2026-04-27NCT02014415
An Extension Study to Assess Long-Term Safety of Eplontersen in Adults With Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)Nutritional and Metabolic Diseases, amyloidosis, metabolic disease, proteostasis deficienciesEnrolling by invitationPhase 32026-04-17NCT05667493
MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, amyloidosis, cardiomyopathy, cardiovascular disorder, familial amyloid neuropathy, heart disorder, hereditary amyloidosis, hereditary disease, inborn errors of metabolism, metabolic disease, proteostasis deficienciesRecruitingPhase 32026-03-27NCT06128629
A Study to Learn About the Safety of Litifilimab (BIIB059) Injections and Whether They Can Improve Symptoms of Adult Participants Who Have Systemic Lupus ErythematosusSkin and Connective Tissue Diseases, autoimmune disease, connective tissue disorder, immune system disorder, systemic lupus erythematosusActive, not recruitingPhase 32026-01-29NCT04961567
Clinical Transcriptomics in Systemic Vasculitis (CUTIS)Cerebral Small Vessel Diseases, Cryoglobulinemic vasculitis, Granuloma, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Skin Manifestations, Skin and Connective Tissue Diseases, anti-neutrophil cytoplasmic antibody-associated vasculitis, arteritis, autoimmune disease, blood coagulation disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, drug-induced vasculitis, eosinophilic granulomatosis with polyangiitis, granulomatosis with polyangiitis, hematologic disorder, hemorrhagic disease, immune system disorder, immunoglobulin A vasculitis, interstitial lung disease, lung disorder, lymphatic system disorder, lymphoproliferative syndrome, microscopic polyangiitis, necrotizing vasculitis, nervous system disorder, polyarteritis nodosa, purpura, respiratory system disorder, skin disorder, skin vascular disease, type III hypersensitivity disease, vascular disorder, vascular hemostatic disease, vasculitisRecruitingNot stated2026-01-22NCT03004326
VCRC Tissue RepositoryAortic Arch Syndromes, Cerebral Small Vessel Diseases, Granuloma, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Skin Manifestations, Skin and Connective Tissue Diseases, Takayasu arteritis, anti-neutrophil cytoplasmic antibody-associated vasculitis, aortic disorder, aortitis, arteritis, autoimmune disease, autoimmune disorder of the nervous system, blood coagulation disease, brain disorder, cardiovascular disorder, central nervous system disorder, central nervous system vasculitis, cerebrovascular disorder, cutaneous vasculitis, eosinophilic granulomatosis with polyangiitis, granulomatosis with polyangiitis, hematologic disorder, hemorrhagic disease, immune system disorder, immunoglobulin A vasculitis, interstitial lung disease, lung disorder, lymphatic system disorder, lymphoproliferative syndrome, microscopic polyangiitis, necrotizing vasculitis, nervous system disorder, polyarteritis nodosa, purpura, respiratory system disorder, skin disorder, skin vascular disease, temporal arteritis, type III hypersensitivity disease, vascular disorder, vascular hemostatic disease, vasculitisRecruitingNot stated2026-01-22NCT02967068
A Study to Assess the Long-Term Safety and Efficacy of Eplontersen (Formerly Known as ION-682884, IONIS-TTR-LRx and AKCEA-TTR-LRx) in Patients With Hereditary Transthyretin-Mediated Amyloid PolyneuropathyHereditary Transthyretin-Mediated Amyloid PolyneuropathyActive, not recruitingPhase 32025-12-04NCT05071300