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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Assess the Long-Term Safety and Efficacy of Eplontersen (Formerly Known as ION-682884, IONIS-TTR-LRx and AKCEA-TTR-LRx) in Patients With Hereditary Transthyretin-Mediated Amyloid PolyneuropathyHereditary Transthyretin-Mediated Amyloid PolyneuropathyActive, not recruitingPhase 32025-12-04NCT05071300

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OrganizationsLinked trials
Ionis Pharmaceuticals, Inc.22

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Research sitesCityCountryLinked trials
Boston University School of MedicineBostonUnited States9
Centre Hospitalier Universitaire de ToulouseToulouseFrance2
Centro Hospitalar Universitário do Porto - Hospital Geral de Santo AntonioPortoPortugal2
Centro Hospitalar Universitário Lisboa Norte - Hospital De Santa MariaLisbonPortugal1
Chang Gung Memorial HospitalTaoyuanTaiwan24
China Medical University HospitalTaichungTaiwan88
Fondazione IRCCS Policlinico San MatteoPaviaItaly75
Hospital Clínico San CarlosMadridSpain47
Hospital das Clínicas da Faculdade de Medicina de Ribeirão PretoSão PauloBrazil1
Hospital El CruceSan Juan BautistaArgentina1
Hospital Italiano de Buenos AiresBuenos AiresArgentina25
Hospital Son LlàtzerPalma de MallorcaSpain1
Hospital Universitario Clementino Fraga FilhoBotafogoBrazil1
Hôpital de La TimoneMarseilleFrance13
Indiana University Health University HospitalIndianapolisUnited States28
Instituto de Neurologia de CuritibaCuritibaBrazil1
Instituto FleniBuenos AiresArgentina1
Istanbul Üniversitesi - Istanbul Tip FakültesiIstanbulTurkey (Türkiye)1
Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) - Fondazione Istituto Neurologico Carlo BestaMilanItaly1
Johns Hopkins University Neurology Research OfficeBaltimoreUnited States1
Mayo ClinicScottsdaleUnited States39
National Taiwan University HospitalTaipeiTaiwan174
Norrlands universitetssjukhusUmeåSweden9
Oregon Health and Science UniversityPortlandUnited States382
Perron Institute for Neurological and Translational ScienceMurdochAustralia1