University Hospital Birmingham NHS Foundation Trust
University Hospital Birmingham NHS Foundation Trust
Birmingham, United Kingdom2 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia | Acid-Base Imbalance, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, acidosis disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, propionic acidemia | Recruiting | Phase 1 / Phase 2 | 2026-01-22 | NCT04159103 | |
| AAV Gene Therapy Study for Subjects with PKU | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuria | Active, not recruiting | Phase 1 / Phase 2 | 2024-12-12 | NCT04480567 |