AAV Gene Therapy Study for Subjects with PKU
AAV Gene Therapy Study for Subjects with PKU
Active, not recruiting · NCT04480567 · Registry updated 2024-12-12Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| AAV Gene Therapy Study for Subjects with PKU | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuria | Active, not recruiting | Phase 1 / Phase 2 | 2024-12-12 | NCT04480567 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| BioMarin Pharmaceutical | 32 |
3 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Morristown Medical Center | Morristown | United States | 179 |
| University Hospital Birmingham NHS Foundation Trust | Birmingham | United Kingdom | 2 |
| University of South Florida | Tampa | United States | 65 |