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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Effect of Patiromer in Children Under 12 Years of Age With High Blood Potassium LevelsHyperkalemia, Nutritional and Metabolic Diseases, Water-Electrolyte Imbalance, metabolic diseaseRecruitingPhase 22026-09-25NCT05766839
Pegtibatinase as a Treatment for Patients With Classical Homocystinuria (HCU) (Also Known as the COMPOSE Study)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, brain disorder, central nervous system disorder, connective tissue disorder, hereditary disease, homocystinuria, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorderRecruitingPhase 1 / Phase 22026-08-10NCT03406611