Pegtibatinase as a Treatment for Patients With Classical Homocystinuria (HCU) (Also Known as the COMPOSE Study)
Pegtibatinase as a Treatment for Patients With Classical Homocystinuria (HCU) (Also Known as the COMPOSE Study)
Recruiting · NCT03406611 · Registry updated 2026-08-10Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Pegtibatinase as a Treatment for Patients With Classical Homocystinuria (HCU) (Also Known as the COMPOSE Study) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, brain disorder, central nervous system disorder, connective tissue disorder, hereditary disease, homocystinuria, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder | Recruiting | Phase 1 / Phase 2 | 2026-08-10 | NCT03406611 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Travere Therapeutics, Inc. | 10 |
5 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Ann & Robert H. Lurie Children's Hospital of Chicago | Chicago | United States | 144 |
| Hospital Necker-Enfants Malades, Neurologie Pediatrique | Paris | France | 1 |
| Science 37 - Virtual Site | Morrisville | United States | 3 |
| Sidra Medicine | Doha | Qatar | 2 |
| The Mount Sinai Hospital | New York | United States | 36 |