Ospedale Pediatrico Giovanni XXIII
Ospedale Pediatrico Giovanni XXIII
Bari, Italy4 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Pegtibatinase as a Treatment for Participants With Classical Homocystinuria (HCU) Receiving Standard of Care Treatment | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, brain disorder, central nervous system disorder, connective tissue disorder, hereditary disease, homocystinuria, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder | Recruiting | Phase 3 | 2026-10-08 | NCT06247085 | |
| A Long-term Extension Study to Assess the Long-term Safety and Efficacy of Pegtibatinase Treatment in Participants ≥5 to ≤65 Years of Age With Classical Homocystinuria (HCU) (ENSEMBLE) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, brain disorder, central nervous system disorder, connective tissue disorder, hereditary disease, homocystinuria, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder | Enrolling by invitation | Phase 3 | 2026-05-28 | NCT06431893 | |
| CACP: Study on Camptodactyly - Arthropathy - Coxa Vara - Pericarditis (CACP) Syndrome | Bone Anteversion, Bone Malalignment, Pathologic Processes, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Torsion Abnormality, arthropathy, bone disorder, cardiovascular disorder, coxa vara, disease, heart disorder, musculoskeletal system disorder, pericarditis, syndromic disease | Recruiting | Not stated | 2026-03-16 | NCT07468461 | |
| Multicenter Italian Cohort Study on Tuberculosis in Pediatric Age | Actinomycetales infectious disease, Bacterial Infections and Mycoses, Infections, bacterial infectious disease, disease arising from reactivation of latent virus, gram-positive bacterial infections, latent tuberculosis infection, mycobacterial infectious disease, tuberculosis | Recruiting | Not stated | 2024-03-04 | NCT06289660 |