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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Mucopolysaccharidosis VII Disease Monitoring ProgramCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 7RecruitingNot stated2026-08-27NCT03604835