Mucopolysaccharidosis VII Disease Monitoring Program
Mucopolysaccharidosis VII Disease Monitoring Program
Recruiting · NCT03604835 · Registry updated 2026-08-27Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Mucopolysaccharidosis VII Disease Monitoring Program | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 7 | Recruiting | Not stated | 2026-08-27 | NCT03604835 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Ultragenyx Pharmaceutical Inc | 24 |
14 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Ann & Robert H. Lurie Children's Hospital of Chicago | Chicago | United States | 144 |
| Centre Hospitalier Universitaire La Timone | Marseille | France | 1 |
| Centro Hospitalar do Porto | Porto | Portugal | 1 |
| Children'S Hospital of Orange County | Orange | United States | 128 |
| Children's National Health System | Washington D.C. | United States | 19 |
| Erasmus University Medical Center Rotterdam | Rotterdam | Netherlands | 1 |
| Hospital de Clínicas de Porto Alegre | Porto Alegre | Brazil | 2 |
| Hospital Universitario Virgen del Rocío Pabellón Infantil | Seville | Spain | 1 |
| Laboratorio de Neuroquimica Dr. N.A. Chamoles S.R.L. | Buenos Aires | Argentina | 1 |
| New York University Langone Medical Center | New York | United States | 23 |
| Seattle Children's Hospital | Seattle | United States | 281 |
| University of Michigan | Ann Arbor | United States | 538 |
| University of Utah Medical Center | Salt Lake City | United States | 3 |
| Universitätsmedizin der Johannes Gutenberg-Universität Mainz | Mainz | Germany | 23 |