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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuriaRecruitingPhase 1 / Phase 22026-08-18NCT06332807