AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)
AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)
Recruiting · NCT06332807 · Registry updated 2026-08-18Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuria | Recruiting | Phase 1 / Phase 2 | 2026-08-18 | NCT06332807 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| NGGT INC. | 1 |
5 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Atlantic Health System | Morristown | United States | 17 |
| Children's Hospital of Orange County Hospital | Orange | United States | 1 |
| University of Minnesota | Minneapolis | United States | 30 |
| University of Pittsburgh Medical Center | Pittsburgh | United States | 18 |
| University or Texas, Southwestern medical Center | Dallas | United States | 1 |