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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuriaRecruitingPhase 1 / Phase 22026-08-18NCT06332807

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OrganizationsLinked trials
NGGT INC.1

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Research sitesCityCountryLinked trials
Atlantic Health SystemMorristownUnited States17
Children's Hospital of Orange County HospitalOrangeUnited States1
University of MinnesotaMinneapolisUnited States30
University of Pittsburgh Medical CenterPittsburghUnited States18
University or Texas, Southwestern medical CenterDallasUnited States1