Ann Robert H. Lurie Children's Hospital of Chicago
Ann Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, United States1 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Juvenile Spinal Muscular Atrophy, Muscular Atrophy, Spinal, Type II, Spinal Muscular Atrophies of Childhood, Spinal Muscular Atrophy Type I, central nervous system disorder, hereditary disease, inherited neurodegenerative disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proximal spinal muscular atrophy, spinal cord disorder, spinal muscular atrophy | Active, not recruiting | Phase 3 | 2026-09-24 | NCT04042025 |