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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioiCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Juvenile Spinal Muscular Atrophy, Muscular Atrophy, Spinal, Type II, Spinal Muscular Atrophies of Childhood, Spinal Muscular Atrophy Type I, central nervous system disorder, hereditary disease, inherited neurodegenerative disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proximal spinal muscular atrophy, spinal cord disorder, spinal muscular atrophyActive, not recruitingPhase 32026-09-24NCT04042025

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OrganizationsLinked trials
Novartis Gene Therapies2

31 results · Page 1 of 2

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Research sitesCityCountryLinked trials
Ann Robert H. Lurie Children's Hospital of ChicagoChicagoUnited States1
Boston Children's HospitalBostonUnited States343
Centre de Référence des Maladies NeuromusculairesLiègeBelgium1
Children's Health Specialty Center Dallas CampusDallasUnited States1
Children's Hospital ColoradoAuroraUnited States312
Children's Hospital of Eastern Ontario Research InstituteOttawaCanada1
Children's Hospital of PhiladelphiaPhiladelphiaUnited States434
Children's Hospital of The King's DaughtersNorfolkUnited States87
Clinic for Special ChildrenStrasburgUnited States2
Columbia University Medical centerNew YorkUnited States224
Duke UniversityDurhamUnited States3
Fondazione Policlinico Universitario Agostino GemelliRomaItaly2
Great Ormond Street Hospital for Children NHS Foundation TrustLondonUnited Kingdom1
Hôpital Armand TrousseauParisFrance7
Instituto Gianninia GasliniGenovaItaly1
Istituto Neurologico di RicercaMilanItaly1
John Hopkins Hospital - David M. Rubenstein Child Health BuildingBaltimoreUnited States1
Massachusetts General HospitalBostonUnited States1015
National Taiwan University HospitalTaipeiTaiwan32
Nationwide Children's HospitalColumbusUnited States309
Spectrum Health Hospitals Helen DeVos Children's HospitalGrand RapidsUnited States1
Stanford University Medical CenterPalo AltoUnited States28
Sydney Children's HospitalRandwickAustralia1
The Newcastle upon Tyne Hospitals NHS Foundation TrustNewcastle upon TyneUnited Kingdom4
Tokyo Women's Medical University HospitalTokyoJapan6