2 results ยท Page 1 of 1

Swipe the table sideways for more columns.

TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of Sepiapterin in Participants With Phenylketonuria (PKU)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuriaRecruitingPhase 32026-08-28NCT06302348
A Study to Assess the Efficacy and Safety of Weekly Doses of GLM101 in Participants With PMM2-CDGDyskinesias, Neurologic Manifestations, PMM2-congenital disorder of glycosylation, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, atactic disorder, non-human animal, nervous system disorderActive, not recruitingPhase 2 / Phase 32026-08-14NCT06892288