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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of Sepiapterin in Participants With Phenylketonuria (PKU)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuriaRecruitingPhase 32026-08-28NCT06302348

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OrganizationsLinked trials
PTC Therapeutics8

10 results · Page 1 of 1