10 results ยท Page 1 of 1

Swipe the table sideways for more columns.

TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Platform of Randomized Adaptive Clinical Trials in Critical IllnessRespiration Disorders, respiratory failure, respiratory system disorderRecruitingNot applicable2026-10-06NCT05440851
A Phase 1b, Open-Label Study of DISC-3405 in Participants With Sickle Cell Disease (SCD)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseRecruitingPhase 12026-10-05NCT07187973
Follow-up Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR GeneX-Linked Retinitis PigmentosaActive, not recruitingPhase 32026-09-25NCT04794101
Periprosthetic Joint Infection Bubble StudyPeriprosthetic Joint Infection (PJI)RecruitingPhase 22026-09-23NCT07599865
An Evaluation of the AeriSeal System for CONVERTing Collateral Ventilation Status in Patients With Severe EmphysemaChronic Disease, Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, chronic obstructive pulmonary disease, lung disorder, obstructive lung disease, pulmonary emphysema, respiratory system disorderRecruitingNot applicable2026-09-17NCT06035120
A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorder, neuromuscular diseaseRecruitingPhase 1 / Phase 22026-07-20NCT07282847
INdependence Through Endovascular Neuroprosthetic Technology (INTENT): an Early Feasibility StudyNutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderRecruitingNot applicable2026-05-11NCT07543367
Understanding the Long-term Impact of COVID on Children and FamiliesCOVID-19, Coronaviridae Infections, Infections, Nidovirales infectious disease, Orthocoronavirinae infectious disease, RNA Virus Infections, lung disorder, pneumonia, respiratory system disorder, respiratory tract infectious disorder, viral infectious disease, viral pneumoniaActive, not recruitingNot stated2025-12-31NCT05172011
Posterior Cervical Fixation StudyBone Diseases, Developmental, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniocervical Injuries, Klippel-Feil syndrome, Musculoskeletal Abnormalities, Radiculopathy, Cervical, Thoracic Injuries, bone disorder, dysostosis, injury, intervertebral disk degenerative disorder, musculoskeletal system disorder, nervous system disorder, nervous system injury, neuromuscular disease, peripheral nervous system disorder, radiculopathy, vertebral column disorderEnrolling by invitationNot stated2025-12-22NCT04770571
Open-Label Safety Study of Acoramidis (AG10) in Symptomatic ATTR ParticipantsAmyloid Neuropathies, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, amyloidosis, familial amyloid neuropathy, hereditary amyloidosis, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, proteostasis deficienciesActive, not recruitingPhase 32025-10-14NCT04988386