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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Open-Label Safety Study of Acoramidis (AG10) in Symptomatic ATTR ParticipantsAmyloid Neuropathies, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, amyloidosis, familial amyloid neuropathy, hereditary amyloidosis, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, proteostasis deficienciesActive, not recruitingPhase 32025-10-14NCT04988386

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OrganizationsLinked trials
Eidos Therapeutics, a BridgeBio company6

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Research sitesCityCountryLinked trials
Aarhus Universitets HospitalAarhus NDenmark1
Alexandra General Hospital of AthensAthensGreece2
Algemeen Ziekenhuis Sint-Jan Brugge-Oostende - Campus Sint-JanBrugesBelgium1
Azienda Ospedaliero - Universitaria CareggiFlorenceItaly4
Boston University Medical Center General Clinical Research UnitBostonUnited States1
Box Hill HospitalBox HillAustralia43
Cedars-Sinai Medical CenterLos AngelesUnited States392
Centre de Recherche du Centre Hospitalier de l'Université de Montréal (CHUM)MontrealCanada1
Centro Avançado de Pesquisa e Estudos para o Diagnóstico CAPEDRibeirão PretoBrazil1
Centro Hospitalar Universitário Lisboa Norte EPE- Hospital Santa MariaLisbonPortugal1
Cleveland Clinic Main CampusClevelandUnited States30
Clinica Universidad de Navarra MadridMadridSpain2
Clínica Universidad de NavarraPamplonaSpain16
Columbia University Irving Medical CenterNew YorkUnited States234
Complejo Hospitalario Universitario de Santiago (CHUS)Santiago de CompostelaSpain1
Duke University Health System - Duke ClinicDurhamUnited States1
Fakultní Nemocnice u sv. Anny v BrněBrnoCzechia2
Fiona Stanley HospitalMurdochAustralia56
Fondazione IRCCS Policlinico San MatteoPaviaItaly75
Fondazione Toscana Gabriele Monasterio per la Ricerca Medica e di Sanità PubblicaPisaItaly1
Hadassah University Hospital Ein KeremJerusalemIsrael5
Hospital Clínico Universitario de ValenciaValenciaSpain17
Hospital Son LlàtzerPalma de MallorcaSpain1
Hospital Universitario Puerta de Hierro - MajadahondaMajadahondaSpain11
Hôpital du Sacré-Coeur de MontréalMontrealCanada2