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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic DisordersCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Embolism and Thrombosis, Hemic and Lymphatic Diseases, Skin and Connective Tissue Diseases, X-linked disease, anemia, blood coagulation disease, blood platelet disease, cardiovascular disorder, coagulation protein disease, connective tissue disorder, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hemophilia A, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, inherited hemoglobinopathy, sickle cell disease, thalassemia, thrombophilia, thrombotic disease, vascular disorder, vascular hemostatic disease, von Willebrand disease (hereditary or acquired)RecruitingNot stated2026-08-17NCT04398628
A Study Assessing HMB-002 in Participants With Von Willebrand DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, coagulation protein disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, von Willebrand disease (hereditary or acquired), von Willebrand disease 3RecruitingPhase 1 / Phase 22026-06-30NCT06754852
Study of Individuals Affected With HypoplasminogenemiahypoplasminogenemiaRecruitingNot stated2026-06-04NCT03797495
A Study of Bleeding and Treatment in Participants With Von Willebrand DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, coagulation protein disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, von Willebrand disease (hereditary or acquired), von Willebrand disease 2, von Willebrand disease 3, von Willebrand disease type 2A, von Willebrand disease type 2M, von Willebrand disease type 2NRecruitingNot stated2026-04-21NCT06610201
A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, cardiovascular disorder, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, vascular disorder, vascular hemostatic diseaseEnrolling by invitationNot stated2026-01-12NCT05768386
Emicizumab in Patients With Acquired Hemophilia Aacquired hemophilia AActive, not recruitingPhase 22025-11-05NCT05345197
Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia ACongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderActive, not recruitingNot stated2024-11-29NCT03432520