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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia ACongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderActive, not recruitingNot stated2024-11-29NCT03432520

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OrganizationsLinked trials
Spark Therapeutics, Inc.4

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Research sitesCityCountryLinked trials
Boston Children's HospitalBostonUnited States343
Hemophilia Center of Western PennsylvaniaPittsburghUnited States7
Mississippi Center for Advanced MedicineMadisonUnited States7
Oregon Health & Science UniversityPortlandUnited States261
Pennsylvania State University Milton S. Hershey Medical CenterHersheyUnited States1
Royal Prince Alfred Hospital Department of Cell & Molecular TherapiesSydneyAustralia1
St. Michael's HospitalTorontoCanada62
The Alfred Hospital & Monash Medical CentreMelbourneAustralia1
The Children's Hospital of PhiladelphiaPhiladelphiaUnited States62
Thomas Jefferson UniversityPhiladelphiaUnited States165
Truman Medical CentersKansas CityUnited States18
Virginia Commonwealth UniversityRichmondUnited States156