Texas Children's Hospital (Baylor College of Medicine)
Texas Children's Hospital (Baylor College of Medicine)
Houston, Texas, United States4 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Phase 1/2 Study of FRF-001, an AAV-9 Gene Therapy, in Patients With FOXG1 Syndrome (FS) | FOXG1 disorder | Enrolling by invitation | Phase 1 / Phase 2 | 2026-07-24 | NCT07293546 | |
| Primary Sclerosing Cholangitis in Children | Cholangitis, Sclerosing, Digestive System Diseases, bile duct disorder, biliary tract disorder, cholangitis, liver disorder, primary sclerosing cholangitis | Recruiting | Not stated | 2026-07-14 | NCT04181138 | |
| Biliary Atresia Study in Infants and Children | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Abnormalities, Digestive System Diseases, bile duct disorder, biliary atresia, biliary tract disorder, cholestasis | Recruiting | Not stated | 2026-06-04 | NCT00345553 | |
| Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency | congenital disorder of deglycosylation 1 | Active, not recruiting | Phase 3 | 2026-05-04 | NCT06199531 |