Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency
Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency
Active, not recruiting · NCT06199531 · Registry updated 2026-05-04Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency | congenital disorder of deglycosylation 1 | Active, not recruiting | Phase 3 | 2026-05-04 | NCT06199531 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Grace Science, LLC | 1 |
2 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Oakland Children's Hospital (UCSF Benioff) | Oakland | United States | 1 |
| Texas Children's Hospital (Baylor College of Medicine) | Houston | United States | 4 |