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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
(PIONEER) Study to Evaluate Efficacy and Safety of Avapritinib (BLU-285), A Selective KIT Mutation-targeted Tyrosine Kinase Inhibitor, Versus Placebo in Patients With Indolent Systemic MastocytosisMast Cell Activation Disorders, Mastocytosis, Systemic, Neoplasms by Histologic Type, Neoplasms, Connective and Soft Tissue, connective tissue neoplasm, immune system disorder, indolent systemic mastocytosis, mastocytosis, neoplasmActive, not recruitingPhase 22026-10-02NCT03731260
International Cooperative Treatment Protocol for Children and Adolescents With Lymphoblastic LymphomaHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingPhase 32026-05-06NCT04043494
Long-term Safety and Tolerability of BHV-7000Drug Resistant Epilepsy, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, central nervous system disorder, epilepsy, focal epilepsy, nervous system disorder, visual epilepsyEnrolling by invitationPhase 22026-05-01NCT06443463
Prospective Observational Study of Filgotinib in Subjects With Rheumatoid ArthritisSkin and Connective Tissue Diseases, arthritic joint disease, arthropathy, autoimmune disease, connective tissue disorder, immune system disorder, musculoskeletal system disorder, rheumatic disorder, rheumatoid arthritisActive, not recruitingNot stated2025-09-15NCT04871919
Observational Study in Patients With Cyclin-dependent Kinase-like 5 Deficiency DisorderEpilepsies, Myoclonic, Epilepsy, Generalized, Epileptic Syndromes, brain disorder, central nervous system disorder, epilepsy, nervous system disorderActive, not recruitingNot stated2025-03-10NCT05373719
Trial to Compare Different Strategies of Mean Arterial Pressure Management During Cardiopulmonary By-passHeart; Surgery, Heart, Functional Disturbance as ResultRecruitingNot applicable2023-02-23NCT05740397