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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
(PIONEER) Study to Evaluate Efficacy and Safety of Avapritinib (BLU-285), A Selective KIT Mutation-targeted Tyrosine Kinase Inhibitor, Versus Placebo in Patients With Indolent Systemic MastocytosisMast Cell Activation Disorders, Mastocytosis, Systemic, Neoplasms by Histologic Type, Neoplasms, Connective and Soft Tissue, connective tissue neoplasm, immune system disorder, indolent systemic mastocytosis, mastocytosis, neoplasmActive, not recruitingPhase 22026-10-02NCT03731260

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OrganizationsLinked trials
Blueprint Medicines Corporation9

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Research sitesCityCountryLinked trials
A.O. OO.RR. S.Giovanni di Dio e Ruggi d'Aragona, University of SalernoSalernoItaly1
A.O.U di Bologna - IRCCS, Istituto di Ematologia Lorenzo e Ariosto Seragnoli, EmatologiaBolognaItaly1
Akademiska sjukhuset, Hematologmottagningen/101AUppsalaSweden1
Azienda Ospedaliera Universitaria Integrata di VeronaVeronaItaly6
Brigham & Women's HospitalBostonUnited States36
Charité Universitätsmedizin BerlinBerlinGermany6
CHU Toulouse Larrey, CEREMAST, Service de Dermatologie et Allergologie cutanéeToulouseFrance1
Clatterbridge Cancer Centre NHS Foundation TrustMetropolitan Borough of WirralUnited Kingdom1
Dana Farber Cancer InstituteBostonUnited States300
Duke University Health System (DUHS)DurhamUnited States1
Erasmus Medical CenterRotterdamNetherlands12
Fondazione IRCCS Ca' Granda Ospedale Maggiore Poloclinico, UOC EmatologiaMilanItaly1
Guy's and St Thomas' NHS Foundation Trust - Guy's HospitalLondonUnited Kingdom5
H. Lee Moffitt Cancer CenterTampaUnited States13
Herbert Irving Comprehensive Cancer CenterNew YorkUnited States6
Hospital Universitari Vall d'HebronBarcelonaSpain200
Huntsman Cancer InstituteSalt Lake CityUnited States107
Hôpital de la Timone, Service de dermatologieMarseilleFrance1
Hôpital Pitié-Salpêtrière, Service de DermatologieParisFrance1
Karolinska University Hospital, Hematologimottagningen R51StockholmSweden1
Klinikum rechts der Isar, Technische Universität MünchenMunichGermany1
lnstituto de Estudios de Mastocitosis de Castilla la Mancha, Hospital Virgen del Valle - Complejo Hospitalario de ToledoToledoSpain1
Mayo ClinicRochesterUnited States664
Mayo Clinic FloridaJacksonvilleUnited States105
Mayo Clinic HospitalPhoenixUnited States41