Sheffield Children's NHS Foundation Trust
Sheffield Children's NHS Foundation Trust
Sheffield, United Kingdom10 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Setrusumab vs Placebo for Osteogenesis Imperfecta | Bone Diseases, Developmental, Collagen Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasia, osteogenesis imperfecta | Active, not recruiting | Phase 2 / Phase 3 | 2026-10-06 | NCT05125809 | |
| Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH) | Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Skin and Connective Tissue Diseases, achondroplasia, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hereditary endocrine growth disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasia | Recruiting | Phase 2 | 2026-07-13 | NCT07169279 | |
| International Randomised Phase III Clinical Trial in Children With Acute Myeloid Leukaemia | Hemic and Lymphatic Diseases, Neoplasm, Residual, Neoplasms by Histologic Type, Neoplastic Processes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, acute myeloid leukemia, hematologic disorder, leukemia, myeloid leukemia, neoplasm | Active, not recruiting | Phase 3 | 2026-06-29 | NCT02724163 | |
| Multi-omics Study in Citrin Deficiency | Adult-onset citrullinemia type 2 | Active, not recruiting | Not stated | 2026-06-02 | NCT06895746 | |
| Dosing of Steroids for Acute Asthma Given in the Emergency Department - a Pilot Randomised Feasibility Trial of Dexamethasone in Children | acute asthma | Recruiting | Phase 4 | 2026-04-23 | NCT07402707 | |
| JIA Toolbox Feasibility Study | Juvenile Idiopahtic Arthritis | Active, not recruiting | Not applicable | 2026-04-22 | NCT07543575 | |
| The Use of DXA in Scoliosis | Spinal Curvatures, bone disorder, musculoskeletal system disorder, scoliosis, vertebral column disorder | Active, not recruiting | Not applicable | 2026-04-20 | NCT06512038 | |
| A Clinical Trial to Evaluate Safety of Vosoritide in At-risk Infants With Achondroplasia | Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, achondroplasia, bone disorder, endocrine system disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasia | Active, not recruiting | Phase 2 | 2026-03-13 | NCT04554940 | |
| An Extension Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia | Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, achondroplasia, bone disorder, endocrine system disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasia | Active, not recruiting | Phase 3 | 2026-03-13 | NCT03424018 | |
| Enroll -HD: A Prospective Registry Study in a Global Huntington's Disease Cohort | Cognition Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyskinesias, Huntington disease, basal ganglia disorder, brain disorder, central nervous system disorder, choreatic disease, cognitive disorder, dementia, hereditary disease, inherited neurodegenerative disorder, movement disorder, nervous system disorder, neurodegenerative disease, psychiatric disorder | Recruiting | Not stated | 2024-02-28 | NCT01574053 |